rare diseases

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Biotech

Senate bill aims to keep NIH, CDC funds intact

The draft legislation would also keep NIH’s 27 institutes and centers, in opposition to Trump’s consolidation plans.
Gabrielle Masson Aug 4, 2025 11:30am
Model skeleton in an anatomy classroom

Antibody strengthens bones in mice with brittle bone disease

Jul 30, 2025 2:54pm
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FDA snubs Ultragenyx gene therapy over manufacturing issues

Jul 14, 2025 10:16am
relay

Rallybio shifts gears, cashing out of Recursion pact

Jul 8, 2025 8:59am
Graphic image of an arrow nailing the bullseye of a target

Cogent hits primary endpoint, building case for Blueprint rival

Jul 7, 2025 9:16am
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Senate revives Orphan Cures Act in Trump's tax bill

Jun 30, 2025 10:09am